Lecturer: Prof. Patrick Onghena – KU Leuven, Belgium.
The objectives of the lecture are:
- To present replicated N-of-1 RCTs as an option to test evidence-based treatments for patients with rare diseases.
- To discuss the advantages and disadvantages of replicated N-of-1 RCTs for rare diseases.
- To demonstrate the use of simple and sound statistical methods for the analysis of data collected in N-of-1 RCTs and replicated N-of-1 RCTs.
