Tag: Early diagnosis

“I hope ERDERA solidifies the mindset that no single group—be it clinicians, patients, researchers, public authorities, or private entities—can succeed alone”

“Knowing there’s a place where someone will listen, understand, and guide you towards what’s best for your child is invaluable.”

EMA warns of unregulated advanced therapies in the EU

Irene Norstedt: “The EU supports collaboration because no country alone, and no stakeholder alone, has the answer for such huge unmet needs in rare disease research”

RE(ACT) Congress 2025 Concludes with Calls for Stronger Collaboration on Rare Diseases

ERDERA: Transforming Rare Disease Research in Europe