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About ERDERA
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Wiskott-Aldrich syndrome (WAS)
Tag: Wiskott-Aldrich syndrome (WAS)
First Italian-made gene therapy for Wiskott-Aldrich Syndrome
December 15, 2025
On 13 November in Milan, EMA’s expert committee backs Italy’s first home‑grown gene therapy for people in Europe living with Wiskott–Aldrich Syndrome.
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About
About ERDERA
Rare Disease Dashboard
Beneficiaries and Participants
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Living with rare
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