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About
About ERDERA
Rare Disease Dashboard
Beneficiaries and Participants
Structure and Governance
Who we are
Privacy Policy
Living with rare
Research Services
Funding
Clinical Research Network
Data Hub
Expertise services
Erdera accelerator
Training and education
International Alignment
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Rare Diseases
Tag: Rare Diseases
A first in personalised medicine: CRISPR treatment for a baby sparks new debate on rare disease therapies
September 24, 2025
Clinical Research
ERDERA
ERDERA Clinical Research Network Jamboree: Including underrepresented countries into innovative diagnostic research
September 24, 2025
Clinical Research
ERDERA
“Data is the fuel of ERDERA’s mission to enhance our insights in rare diseases, to expedite diagnosis, and to find new treatments”
August 20, 2025
ERDERA interviews Ronald Cornet
Data Hub
Patients as equal partners – ERDERA’s vision echoes in Brussels
July 10, 2025
Clinical Research
Patient Involvement (PPIE)
Scientific Coordinator Daria Julkowska contributes to Science Magazine and Ipsen Foundation’s high-level webinar on rare disease research collaboration
July 2, 2025
Clinical Research
“There’s a lot of value in connecting with other countries — learning what has worked, what hasn’t, and applying those lessons”
June 11, 2025
International Alignment
Patient Involvement (PPIE)
Triplet repeat expansion project sets benchmark for public-private collaboration
June 11, 2025
Accelerator
Clinical Research
Expertise Services
“The National Mirror Group was the first time patients had been treated as equal partners in this kind of forum, and it immediately changed the conversation”
June 4, 2025
International Alignment
Patient Involvement (PPIE)
Europe’s rare-disease alliance charts next steps at Riga workshop
June 3, 2025
International Alignment
ERDERA’s Networking Support Scheme opens to forge new rare disease and rare cancer alliances
May 29, 2025
Funding
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About
About ERDERA
Rare Disease Dashboard
Beneficiaries and Participants
Structure and Governance
Who we are
Privacy Policy
Living with rare
Research Services
Funding
Clinical Research Network
Data Hub
Expertise services
Erdera accelerator
Training and education
International Alignment
News & Updates
Resources
RD Virtual Platform
ERN consented forms