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About
About ERDERA
Rare Disease Dashboard
Beneficiaries and Participants
Structure and Governance
Who we are
Privacy Policy
Living with rare
Research Services
ERDERA Funding
Clinical Research
Data Hub
Expertise services
Erdera accelerator
Training and education
International Alignment
News & Updates
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RD Virtual Platform
ERN consented forms
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ATMPs
Tag: ATMPs
A first in personalised medicine: CRISPR treatment for a baby sparks new debate on rare disease therapies
September 24, 2025
Clinical Research
ERDERA
Multi stakeholder workshop advances prioritisation of rare diseases for ATMP development
September 17, 2025
A practical framework in the making
Accelerator
Clinical Research
Data Hub
Expertise Services
Patient Involvement (PPIE)
EU rare disease conference concludes in Warsaw with renewed focus on early diagnosis and collaborative research
April 14, 2025
Clinical Research
International Alignment
Patient Involvement (PPIE)
Rare Disease conference kicks off in Warsaw: Building momentum for a unified EU strategy
April 10, 2025
Rare disease experts to gather in Warsaw to shape Europe’s future strategy
March 27, 2025
Accelerator
EMA warns of unregulated advanced therapies in the EU
March 21, 2025
Expertise Services
International Alignment
RE(ACT) Congress and IRDiRC Conference 2025 concludes with calls for stronger collaboration on rare diseases
March 7, 2025
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About
About ERDERA
Rare Disease Dashboard
Beneficiaries and Participants
Structure and Governance
Who we are
Privacy Policy
Living with rare
Research Services
ERDERA Funding
Clinical Research
Data Hub
Expertise services
Erdera accelerator
Training and education
International Alignment
News & Updates
Resources
RD Virtual Platform
ERN consented forms