Tag: ATMPs

A first in personalised medicine: CRISPR treatment for a baby sparks new debate on rare disease therapies

Multi stakeholder workshop advances prioritisation of rare diseases for ATMP development

A practical framework in the making

EU rare disease conference concludes in Warsaw with renewed focus on early diagnosis and collaborative research

Rare Disease conference kicks off in Warsaw: Building momentum for a unified EU strategy

Rare disease experts to gather in Warsaw to shape Europe’s future strategy

EMA warns of unregulated advanced therapies in the EU

RE(ACT) Congress and IRDiRC Conference 2025 concludes with calls for stronger collaboration on rare diseases