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Bridging the gap between scientific discovery and investment-ready innovation for rare disease breakthroughs.

ERDERA Technology Accelerator

The ERDERA Technology Accelerator advances the enabling technologies that make rare-disease therapies possible. We bring public and private partners together to mature, validate, and streamline advanced therapy platforms so promising discoveries can move faster, safer, and more efficiently toward the clinic.

By strengthening shared technological toolboxes for the rare disease community, we help reduce development risk and accelerate translation across multiple indications.

You are a technology developer…

…working on enabling technologies for rare-disease therapies within academia, a research infrastructure, an SME, or industry.

…developing platforms such as viral or non-viral delivery systems, gene-editing tools, therapeutic RNAs, or analytical and manufacturing solutions.

…looking to improve robustness, scalability, comparability, or clinical relevance of your technology through collaboration and real-world feedback.

If this sounds like you, the Technology Accelerator can help.

 

The Technology Accelerator supports partners by:

Advancing enabling ATMP technologies, including:

Adeno-associated Virus (AAVs)

Messenger RNA (mRNA)

Lipid Nanoparticles, Extracellular Vesicles, Biohybrids

Gene Editing Tools

Addressing key technical bottlenecks across:

Delivery efficiency and tissue targeting

Manufacturing and scale-up

Analytical characterisation and quality control

Evaluation of therapy response, safety, and immunogenicity

Facilitating pre-competitive collaboration between public and private stakeholders to strengthen shared technology platforms.

Aligning technology development with translational and clinical needs in rare diseases.

Advancing enabling ATMP technologies, including:

  • Adeno-associated Virus (AAVs)
  • Messenger RNA (mRNA)
  • Lipid Nanoparticles, Extracellular Vesicles, Biohybrids
  • Gene Editing Tools

Addressing key technical bottlenecks across:

  • Delivery efficiency and tissue targeting
  • Manufacturing and scale-up
  • Analytical characterisation and quality control
  • Evaluation of therapy response, safety, and immunogenicity

Networking

Facilitating pre-competitive collaboration between public and private stakeholders to strengthen shared technology platforms.

Alignment

Aligning technology development with translational and clinical needs in rare diseases.

Robust, well-validated enabling technologies are essential for translating rare-disease discoveries into viable therapies. By strengthening these foundations, the Technology Accelerator supports not just individual projects but the entire rare-disease innovation ecosystem.

Understand the concept of ATMPs with this Knowledge Pill

The role of National Mirror Groups (NMGs)

This 2025 country report outlines the policy, research, care and support landscape for rare diseases in Cyprus.
Model award agreement document setting out the structure, articles and contractual provisions applicable to funded activities.
This annex explains the specific eligibility, sponsorship, funding and application requirements for Canadian applicants in the ERDERA Clinical Trial Call.
Call text draft setting out rules, eligibility and staged application process for the ERDERA Clinical Trial Call 2026.

Latest relevant publications

Model award agreement document setting out the structure, articles and contractual provisions applicable to funded activities.
This annex explains the specific eligibility, sponsorship, funding and application requirements for Canadian applicants in the ERDERA Clinical Trial Call.
Call text draft setting out rules, eligibility and staged application process for the ERDERA Clinical Trial Call 2026.
The multicentre observational study analysed 661 assessments from 219 people with SCA27B to examine disease progression, clinical outcome metrics and demographic or genetic modifiers.